FcRn PK/PD

Efgartigimod FcRn Kinetics & Myositis Trial Simulator

Clinical & Regimen Controls Regimen Active
Endosomal FcRn Blockade Flux Blockade: 88%
Early Endosome (pH 6.0) Lysosome Degradation Extracellular (pH 7.4)
■ Efgartigimod (Fc-fragment) out-competes endogenous ● Pathogenic IgG for FcRn binding at pH 6.0, shunting free IgG into lysosomal catabolism.
Total IgG Clearance & Clinical Total Improvement Score (TIS)
Total IgG Pathogenic Autoantibody TIS Score
Peak IgG Reduction
64.2%
Nadir: 4.4 g/L
Autoantibody Half-Life (t½)
3.8 days
Normal IgG t½: 21.0 d
Degradation Flux Increase
3.2x
Target Occupancy: 88%
Predicted TIS (Week 8)
42.6
Moderate Improvement (≥40)
Primary Efficacy Endpoint (TIS ≥ 20 at Wk 8/12): MET (p < 0.001)
ΔTIS vs Placebo: +24.1 pts
Comparative Mechanism Benchmark (Myositis)
Modality Target Mechanism Onset Speed IgG Depletion Infection Risk
Efgartigimod (FcRn) Selective IgG recycling blockade Rapid (1–2 wks) ~65% selective Low (IgA/M spared)
IVIg (High Dose) FcRn saturation + scavenging Moderate (2–4 wks) Indirect (~30%) Moderate (Volume load)
Rituximab (Anti-CD20) B-cell lineage depletion Delayed (8–16 wks) De novo synthesis Elevated (Prolonged)
Pulsed Steroids Broad NF-κB transcription block Rapid (Days) Non-specific High (Metabolic/Infect.)
Clinical Trial Dossier & Kinetic Summary

Source Context: Grounded in Argenx's Phase 2/3 idiopathic inflammatory myopathy trial readouts across Dermatomyositis (DM), Polymyositis (PM), and Necrotizing Myopathy (IMNM).

Pathophysiological Note: Accelerating IgG catabolism by clearing the neonatal Fc receptor reduces pathogenic autoantibodies (anti-Mi-2, anti-Jo-1, anti-SRP) without triggering generalized immunosuppression.

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